Sickle cell gene therapies approach watershed

Nature Biotechnology
Volume 39 Issue 11, November 2021


News | 09 November 2021
Sickle cell gene therapies approach watershed
Early results promise a one-off treatment, but gene-editing and gene therapies will have to show durable protection and be affordable to the many patients with sickle cell disease in the world.
Cormac Sheridan