Nature Reviews Drug Discovery
Volume 19 Issue 8, August 2020
Comment | 20 April 2020
Boosting delivery of rare disease therapies: the IRDiRC Orphan Drug Development Guidebook
The International Rare Diseases Research Consortium (IRDiRC) has created a Guidebook to facilitate drug development for rare diseases by organizing available tools into a standardized framework.
Anneliene Hechtelt Jonker, Virginie Hivert[…] & Diego Ardigo