Gene Editing for the Treatment of Primary Immunodeficiency Diseases

Human Gene Therapy
Volume 32, Issue 1-2 / January 2021
https://www.liebertpub.com/toc/hum/32/1-2

 

Reviews Open Access
Gene Editing for the Treatment of Primary Immunodeficiency Diseases
Rajeev Rai, Adrian J. Thrasher, and Alessia Cavazza
Pages:43–51
Published Online:16 October 2020
https://doi.org/10.1089/hum.2020.185
With conventional treatments for primary immunodeficiency diseases (PIDs), such as allogeneic stem cell transplantation or autologous gene therapy, still facing important challenges, the rapid development of genome editing technologies to more accurately …